Treatment options are available to help manage the signs and symptoms of
Gaucher disease, including oral therapy. The goal of treatment is to reduce or
prevent the build-up of GL-1.
patient with Gaucher disease type 1 treated with Cerdelga
While there is no cure, if you have been diagnosed with Gaucher disease type 1, treatment approaches are available to manage the disease, including oral medicine. The goal of these treatments is to reduce or prevent the buildup of GL-1. Treatment outcomes may vary among patients.2 treatment approaches for Gaucher disease type 1:
SUBSTRATE REDUCTION THERAPY (SRT)
ENZYME REPLACEMENT THERAPY (ERT)
Most adult patients newly diagnosed with Gaucher disease type 1 can begin treatment with an oral therapy, and it is possible for most adult patients with Gaucher disease type 1 currently being treated with an ERT (infusion) to switch to an oral therapy. Your doctor will know the best course of treatment for you.